Page Title
Drug Development Pipeline
Back to the Drug Development Pipeline
Icagen
Status
Pre-clinicalTherapeutic Approach
Restore CFTR Protein
This program is working to identify potential therapies for people with CF who have nonsense mutations. Nonsense mutations (also known as “x” or “stop” mutations) in the CFTR gene cause the production of CFTR protein to stop prematurely. Overriding these premature stop signals would allow full-length, functional CFTR protein to be made.
Status
Laboratory studies to develop and test these compounds are underway.
Sponsor
This program is sponsored by Icagen Inc. and partially funded by the Cystic Fibrosis Foundation.
Sign up for clinical trial alerts
Get email updates about clinical trials that matter to you.
Explore clinical trials
Be a part of the movement transforming the future of cystic fibrosis treatment.
Learn More